ORIGA, RAFFAELLA
ORIGA, RAFFAELLA
DIPARTIMENTO DI SCIENZE MEDICHE E SANITA' PUBBLICA
Long-term efficacy and safety of luspatercept for the treatment of anaemia in patients with transfusion-dependent β-thalassaemia (BELIEVE): final results from a phase 3 randomised trial
2025-01-01 Domenica Cappellini, Maria; Viprakasit, Vip; Georgiev, Pencho; D Coates, Thomas; Origa, Raffaella; Khelif, Abderrahim; Liew, Hong-Keng; Tantiworawit, Adisak; Chew, Lee-Ping; Khalil, Abdalla; Joy Ho, P; M Kuo, Kevin H; Holot, Natalia; Perin, Martina; Carolina Giuseppi, Ana; Kuo, Wen-Ling; Lai, Yinzhi; Felber Medlin, Loyse; Moro Bueno, Luciana; Kattamis, Antonis; T Taher, Ali
Prevalence and mortality trends of hemoglobinopathies in Italy: a nationwide study
2025-01-01 Gianesin, B; Piel, Fb; Musallam, Km; Barella, S; Casale, M; Cassinerio, E; Di Maggio, R; Gigante, A; Gamberini, Mr; Graziadei, G; Lisi, R; Longo, F; Maggio, A; Origa, R; Pasanisi, A; Perrotta, S; Piga, Ag; Pinto, Vm; Rosso, R; Robello, G; Russo, G; Zecca, M; De Franceschi, L; Forni, Gl
Beta Thalassemia in Children: Established Approaches, Old Issues, New Non-Curative Therapies, and Perspectives on Healing
2024-01-01 Origa, Raffaella; Issa, Layal
Deferasirox film-coated tablet-associated ulcerative colitis: An emerging pattern in thalassemia patients?
2024-01-01 Piolatto, A; Gaglioti, Cm; Tesio, N; Clemente, Mg; Culcasi, M; Matrone, A; Pila, Mp; Sambataro, A; Longo, F; Origa, R; Ferrero, Gb.
Differential effects of iron chelators on iron burden and long-term morbidity and mortality outcomes in a large cohort of transfusion-dependent β-thalassemia patients who remained on the same monotherapy over 10 years
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Phenoconversion’ in adult patients with β-thalassemia
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Revisiting iron overload status and change thresholds as predictors of mortality in transfusion-dependent β-thalassemia: a 10-year cohort study
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Unplanned pregnancy in women with beta-thalassaemia treated with luspatercept
2024-01-01 Zaccheddu, E; Zappu, A; Barella, S; Clemente, Mg; Orecchia, V; Pilia, Mp; Piras, S; Pitturru, C; Scarano, M; Origa, R.
Atrial Fibrillation Prevalence and Its Management in Transfusion-Dependent Thalassemias: The Fathal Study
2023-01-01 Di Stefano, Valeria; Gianesin, Barbara; Bertini, Matteo; Culcasi, Martina; Rita Denotti, Anna; Derchi, Giorgio; Giuditta, Marianna; Longo, Filomena; Regina Manca, Maria; Cristina Martinoli, Maria; Orecchia, Valeria; Origa, Raffaella; Motta, Irene
Hepatitis C and Thalassemia: A Story with (Almost) a Happy Ending
2023-01-01 Origa, Raffaella
Incidence of cancer and related deaths in hemoglobinopathies: A follow-up of 4631 patients between 1970 and 2021
2023-01-01 Origa, Raffaella; Gianesin, Barbara; Longo, Filomena; Di Maggio, Rosario; Cassinerio, Elena; Rita Gamberini, Maria; Maria Pinto, Valeria; Quarta, Antonella; Casale, Maddalena; LA NASA, Giorgio; Caocci, Giovanni; Piroddi, Antonio; Piolatto, Andrea; Di Mauro, Alessandra; Romano, Claudia; Gigante, Antonia; Barella, Susanna; Maggio, Aurelio; Graziadei, Giovanna; Perrotta, Silverio; Luca Forni, Gian
Luspatercept in the Treatment of Beta Thalassemia in Italy: Lights and Shadows in Clinical Practice
2023-01-01 Gianesin, Barbara; Rosso, Rosamaria; Lisi, Roberto; Zappu, Antonietta; Motta, Irene; Longo, Filomena; Pinto, Valeria; Maria Grazia Sanna, Paola; De Franceschi, Lucia; Battista Ruffo, Giovan; DI Maggio, Rosario; Bulla, Anna; Ann Di Giorgio, Mary; Rita Denotti, Anna; Lello Panzieri, Daniele; Culcasi, Martina; Quintino, Sabrina; Marchisio, Andrea; Mazzi, Filippo; Miciotto, Francesca; Barone, Rita; Di Raimondo, Francesco; Ferraresi, Marta; Marchetti, Beatrice; Origa, Raffaella
Management of the Sickle Cell Trait: An Opinion by Expert Panel Members.
2023-01-01 Pinto, Vm; De Franceschi, L; Gianesin, B; Gigante, A; Graziadei, G; Lombardini, L; Palazzi, G; Quota, A; Russo, R; Sainati, L; Venturelli, D; Forni, Gl; Origa, R.
Nephrological Complications in Hemoglobinopathies: SITE Good Practice
2023-01-01 Ruffo, Gb; Russo, R; Casini, T; Lombardini, L; Orecchia, V; Voi, V; Origa, R; Forni, Gl; Marchetti, M; Gigante, A; Garibotto, G; Maggio, A; De Franceschi, L.
Pretransfusion hemoglobin level and mortality in adults with transfusiondependent β-thalassemia
2023-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl.
Reply to "Hepatocellular carcinoma in thalassemia and other hemoglobinopathies"
2023-01-01 Origa, R; Gianesin, B; Longo, F; Di Maggio, R; Cassinerio, E; Gamberini, Mr; Pinto, Vm; Casale, M; La Nasa, G; Caocci, G; Piroddi, A; Piolatto, A; Di Mauro, A; Romano, C; Gigante, A; Barella, S; Maggio, A; Graziadei, G; Perrotta, S; Forni, Gl.
Treating Thalassemia Patients with Luspatercept: An Expert Opinion Based on Current Evidence
2023-01-01 Longo, F; Motta, I; Pinto, V; Piolatto, A; Ricchi, P; Tartaglione, I; Origa, R.
2021 Thalassaemia International Federation Guidelines for the Management of Transfusion-dependent Thalassemia
2022-01-01 Farmakis, D.; Porter, J.; Taher, A.; Cappellini, M. D.; Angastiniotis, M.; Eleftheriou, A.; Alassaf, A.; Angastiniotis, M.; Angelucci, E.; Aydinok, Y.; Bou-Fakhredin Rayan, R.; Brunetta, L.; Cappellini, M. D.; Constantinou, G.; Daar, S.; De Sanctis, V.; Dusheiko, G.; Elbard, R.; Eleftheriou, A.; Eleftheriou, P.; Englezos, P.; Farmakis, D.; Haines, D.; Hattab, F. N.; Kaltsounis, G.; Kattamis, A.; Koskinas, J.; Kumar, N.; Kulozik, A.; Kyriakou, A.; Maggio, A.; Maharai, R.; Mednick, L.; Michalaki, E.; Murphy, W.; Oevermann, L.; Origa, R.; Papayanni, P. -G.; Politis, C.; Porter, J.; Shah, F.; Skafi, A.; Skordis, N.; Sodani, P.; Soliman, A.; Subair, S.; Taher, A.; Tampaki, M.; Trompeter, S.; Tuli, S.; Walker, M.; Yamashita, R.; Yannaki, E.; Yardumian, A.
Crushed deferasirox film-coated tablets in pediatric patients with transfusional hemosiderosis: Results from a single-arm, interventional phase 4 study (MIMAS)
2022-01-01 Wali, Y.; Hassan, T.; Charoenkwan, P.; Trompeter, S.; Tartaglione, I.; Origa, R.; Gamberini, M. R.; Viprakasit, V.; Izquierdo, M.; Opio, S.; Roy, T.; Taher, A.
Good Clinical Practice of the Italian Society of Thalassemia and Haemoglobinopathies (SITE) for the Management of Endocrine Complications in Patients with Haemoglobinopathies
2022-01-01 Casale, M; Baldini, Mi; Del Monte, P; Gigante, A; Grandone, A; Origa, R; Poggi, M; Gadda, F; Lai, R; Marchetti, M; Forni, Gl
Titolo | Data di pubblicazione | Autore(i) | Rivista | Editore |
---|---|---|---|---|
Long-term efficacy and safety of luspatercept for the treatment of anaemia in patients with transfusion-dependent β-thalassaemia (BELIEVE): final results from a phase 3 randomised trial | 1-gen-2025 | Domenica Cappellini, Maria; Viprakasit, Vip; Georgiev, Pencho; D Coates, Thomas; Origa, Raffaella; Khelif, Abderrahim; Liew, Hong-Keng; Tantiworawit, Adisak; Chew, Lee-Ping; Khalil, Abdalla; Joy Ho, P; M Kuo, Kevin H; Holot, Natalia; Perin, Martina; Carolina Giuseppi, Ana; Kuo, Wen-Ling; Lai, Yinzhi; Felber Medlin, Loyse; Moro Bueno, Luciana; Kattamis, Antonis; T Taher, Ali | THE LANCET. HAEMATOLOGY | - |
Prevalence and mortality trends of hemoglobinopathies in Italy: a nationwide study | 1-gen-2025 | Gianesin, B; Piel, Fb; Musallam, Km; Barella, S; Casale, M; Cassinerio, E; Di Maggio, R; Gigante, A; Gamberini, Mr; Graziadei, G; Lisi, R; Longo, F; Maggio, A; Origa, R; Pasanisi, A; Perrotta, S; Piga, Ag; Pinto, Vm; Rosso, R; Robello, G; Russo, G; Zecca, M; De Franceschi, L; Forni, Gl | HAEMATOLOGICA | - |
Beta Thalassemia in Children: Established Approaches, Old Issues, New Non-Curative Therapies, and Perspectives on Healing | 1-gen-2024 | Origa, Raffaella; Issa, Layal | JOURNAL OF CLINICAL MEDICINE | - |
Deferasirox film-coated tablet-associated ulcerative colitis: An emerging pattern in thalassemia patients? | 1-gen-2024 | Piolatto, A; Gaglioti, Cm; Tesio, N; Clemente, Mg; Culcasi, M; Matrone, A; Pila, Mp; Sambataro, A; Longo, F; Origa, R; Ferrero, Gb. | BRITISH JOURNAL OF HAEMATOLOGY | - |
Differential effects of iron chelators on iron burden and long-term morbidity and mortality outcomes in a large cohort of transfusion-dependent β-thalassemia patients who remained on the same monotherapy over 10 years | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | BLOOD CELLS, MOLECULES, & DISEASES | - |
Phenoconversion’ in adult patients with β-thalassemia | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | AMERICAN JOURNAL OF HEMATOLOGY | - |
Revisiting iron overload status and change thresholds as predictors of mortality in transfusion-dependent β-thalassemia: a 10-year cohort study | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | ANNALS OF HEMATOLOGY | - |
Unplanned pregnancy in women with beta-thalassaemia treated with luspatercept | 1-gen-2024 | Zaccheddu, E; Zappu, A; Barella, S; Clemente, Mg; Orecchia, V; Pilia, Mp; Piras, S; Pitturru, C; Scarano, M; Origa, R. | BRITISH JOURNAL OF HAEMATOLOGY | - |
Atrial Fibrillation Prevalence and Its Management in Transfusion-Dependent Thalassemias: The Fathal Study | 1-gen-2023 | Di Stefano, Valeria; Gianesin, Barbara; Bertini, Matteo; Culcasi, Martina; Rita Denotti, Anna; Derchi, Giorgio; Giuditta, Marianna; Longo, Filomena; Regina Manca, Maria; Cristina Martinoli, Maria; Orecchia, Valeria; Origa, Raffaella; Motta, Irene | BLOOD | - |
Hepatitis C and Thalassemia: A Story with (Almost) a Happy Ending | 1-gen-2023 | Origa, Raffaella | PATHOGENS | - |
Incidence of cancer and related deaths in hemoglobinopathies: A follow-up of 4631 patients between 1970 and 2021 | 1-gen-2023 | Origa, Raffaella; Gianesin, Barbara; Longo, Filomena; Di Maggio, Rosario; Cassinerio, Elena; Rita Gamberini, Maria; Maria Pinto, Valeria; Quarta, Antonella; Casale, Maddalena; LA NASA, Giorgio; Caocci, Giovanni; Piroddi, Antonio; Piolatto, Andrea; Di Mauro, Alessandra; Romano, Claudia; Gigante, Antonia; Barella, Susanna; Maggio, Aurelio; Graziadei, Giovanna; Perrotta, Silverio; Luca Forni, Gian | CANCER | - |
Luspatercept in the Treatment of Beta Thalassemia in Italy: Lights and Shadows in Clinical Practice | 1-gen-2023 | Gianesin, Barbara; Rosso, Rosamaria; Lisi, Roberto; Zappu, Antonietta; Motta, Irene; Longo, Filomena; Pinto, Valeria; Maria Grazia Sanna, Paola; De Franceschi, Lucia; Battista Ruffo, Giovan; DI Maggio, Rosario; Bulla, Anna; Ann Di Giorgio, Mary; Rita Denotti, Anna; Lello Panzieri, Daniele; Culcasi, Martina; Quintino, Sabrina; Marchisio, Andrea; Mazzi, Filippo; Miciotto, Francesca; Barone, Rita; Di Raimondo, Francesco; Ferraresi, Marta; Marchetti, Beatrice; Origa, Raffaella | BLOOD | - |
Management of the Sickle Cell Trait: An Opinion by Expert Panel Members. | 1-gen-2023 | Pinto, Vm; De Franceschi, L; Gianesin, B; Gigante, A; Graziadei, G; Lombardini, L; Palazzi, G; Quota, A; Russo, R; Sainati, L; Venturelli, D; Forni, Gl; Origa, R. | JOURNAL OF CLINICAL MEDICINE | - |
Nephrological Complications in Hemoglobinopathies: SITE Good Practice | 1-gen-2023 | Ruffo, Gb; Russo, R; Casini, T; Lombardini, L; Orecchia, V; Voi, V; Origa, R; Forni, Gl; Marchetti, M; Gigante, A; Garibotto, G; Maggio, A; De Franceschi, L. | JOURNAL OF CLINICAL MEDICINE | - |
Pretransfusion hemoglobin level and mortality in adults with transfusiondependent β-thalassemia | 1-gen-2023 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl. | BLOOD | - |
Reply to "Hepatocellular carcinoma in thalassemia and other hemoglobinopathies" | 1-gen-2023 | Origa, R; Gianesin, B; Longo, F; Di Maggio, R; Cassinerio, E; Gamberini, Mr; Pinto, Vm; Casale, M; La Nasa, G; Caocci, G; Piroddi, A; Piolatto, A; Di Mauro, A; Romano, C; Gigante, A; Barella, S; Maggio, A; Graziadei, G; Perrotta, S; Forni, Gl. | CANCER | - |
Treating Thalassemia Patients with Luspatercept: An Expert Opinion Based on Current Evidence | 1-gen-2023 | Longo, F; Motta, I; Pinto, V; Piolatto, A; Ricchi, P; Tartaglione, I; Origa, R. | JOURNAL OF CLINICAL MEDICINE | - |
2021 Thalassaemia International Federation Guidelines for the Management of Transfusion-dependent Thalassemia | 1-gen-2022 | Farmakis, D.; Porter, J.; Taher, A.; Cappellini, M. D.; Angastiniotis, M.; Eleftheriou, A.; Alassaf, A.; Angastiniotis, M.; Angelucci, E.; Aydinok, Y.; Bou-Fakhredin Rayan, R.; Brunetta, L.; Cappellini, M. D.; Constantinou, G.; Daar, S.; De Sanctis, V.; Dusheiko, G.; Elbard, R.; Eleftheriou, A.; Eleftheriou, P.; Englezos, P.; Farmakis, D.; Haines, D.; Hattab, F. N.; Kaltsounis, G.; Kattamis, A.; Koskinas, J.; Kumar, N.; Kulozik, A.; Kyriakou, A.; Maggio, A.; Maharai, R.; Mednick, L.; Michalaki, E.; Murphy, W.; Oevermann, L.; Origa, R.; Papayanni, P. -G.; Politis, C.; Porter, J.; Shah, F.; Skafi, A.; Skordis, N.; Sodani, P.; Soliman, A.; Subair, S.; Taher, A.; Tampaki, M.; Trompeter, S.; Tuli, S.; Walker, M.; Yamashita, R.; Yannaki, E.; Yardumian, A. | HEMASPHERE | - |
Crushed deferasirox film-coated tablets in pediatric patients with transfusional hemosiderosis: Results from a single-arm, interventional phase 4 study (MIMAS) | 1-gen-2022 | Wali, Y.; Hassan, T.; Charoenkwan, P.; Trompeter, S.; Tartaglione, I.; Origa, R.; Gamberini, M. R.; Viprakasit, V.; Izquierdo, M.; Opio, S.; Roy, T.; Taher, A. | AMERICAN JOURNAL OF HEMATOLOGY | - |
Good Clinical Practice of the Italian Society of Thalassemia and Haemoglobinopathies (SITE) for the Management of Endocrine Complications in Patients with Haemoglobinopathies | 1-gen-2022 | Casale, M; Baldini, Mi; Del Monte, P; Gigante, A; Grandone, A; Origa, R; Poggi, M; Gadda, F; Lai, R; Marchetti, M; Forni, Gl | JOURNAL OF CLINICAL MEDICINE | - |