ORIGA, RAFFAELLA
ORIGA, RAFFAELLA
DIPARTIMENTO DI SCIENZE MEDICHE E SANITA' PUBBLICA
A Combination of Plerixafor and Filgrasting Promotes Successful CD34+ Cell Collection for CRISPR/Cas9 Therapy in Sickle Cell Disease Patients With Insufficient Response to Plerixafor Alone.
2026-01-01 Arcioni, F; Bonetti, M; Sau, A; Zecca, M; Alzahrani, M; Alahmari, B; Alsadi, H; Almozaini, A; Ahmed, M; Essa, M; Perotti, C; Del Fante, C; Passeri, C; Iuliani, O; Russo, Ac; Di Ianni, M; Marchesi, M; Pasqua, Bl; Onorato, M; Berchicci, L; Pierini, A; Zei, T; Iacucci, R; Cerri, C; Gurdo, G; Innocente, A; Capolsini, I; Gorello, P; Colombatti, R; Origa, R; Caniglia, M.
Atrial fibrillation prevalence and its management in aging transfusion-dependent thalassemia patients: the FATHAL study
2026-01-01 Di Stefano, V; Gianesin, B; Orecchia, V; Longo, F; Susanna, B; Barone, A; Culcasi, M; Denotti, Ar; Costantini, S; Ferrara, F; Foggetti, I; Gigante, A; Manca, Mr; Mazzi, F; Pasanisi, A; Pisaniello, M; Ricchi, P; Serra, M; Origa, R; Bertini, M; Motta, I.
Pregnancy and childbirth in women with thalassemia: past and present
2026-01-01 Demurtas, A; Gianesin, B; Zappu, A; Cassinerio, E; Leoni, S; Ricchi, P; Fatigati, C; Ruffo, G; Miciotto, F; Roberti, D; Tartaglione, I; Pasanisi, A; Longo, F; Sorrentino, F; Salvo, A; De Franceschi, L; Lisi, R; Murgia, M; Pisano, V; Sanna, P; Testa, E; Atzeni, I; Mariani, R; Valentini, C; Arcioni, F; Barcella, L; Culcasi, M; Vitucci, A; Miulli, E; Pugliese, P; Fotzi, I; Paci, C; Barella, S; Gigante, A; Forni, G; Origa, R
Real-world evidence supports the safety and efficacy profile of luspatercept in clinically complex and heavily iron-overloaded patients
2026-01-01 Gianesin, B; Zappu, A; Ferrero, Gb; Gaglioti, Cm; Santodirocco, M; Fania, G; Graziadei, G; Panzieri, Dl; Massa, A; Mina, T; Polese, F; Vitucci, A; Arcioni, F; Putti, Mc; Cecinati, V; Fotzi, I; Sanna, Pmg; Cappello, A; Longo, F; Lisi, R; Pasanisi, A; Pietrasanta, D; Bocchia, M; Bertoni, E; Cossu, A; Serra, M; Barella, S; Gigante, A; Forni, Gl; Origa, R.
The Emerging Role of Liver Stiffness Measurement in Transfusion Dependent Thalassemia.
2026-01-01 Gianesin, B; Ferrero, Gb; Longo, F; Barella, S; Origa, R; Lisi, R; Pasanisi, A; Bacigalupo, L; De Franceschi, L; Forni, Gl.
Long-term efficacy and safety of luspatercept for the treatment of anaemia in patients with transfusion-dependent β-thalassaemia (BELIEVE): final results from a phase 3 randomised trial
2025-01-01 Domenica Cappellini, Maria; Viprakasit, Vip; Georgiev, Pencho; D Coates, Thomas; Origa, Raffaella; Khelif, Abderrahim; Liew, Hong-Keng; Tantiworawit, Adisak; Chew, Lee-Ping; Khalil, Abdalla; Joy Ho, P; M Kuo, Kevin H; Holot, Natalia; Perin, Martina; Carolina Giuseppi, Ana; Kuo, Wen-Ling; Lai, Yinzhi; Felber Medlin, Loyse; Moro Bueno, Luciana; Kattamis, Antonis; T Taher, Ali
Luspatercept for Transfusion-Dependent Beta-Thalassemia: Real-World Experience in a Large Cohort of Patients From Italy
2025-01-01 Origa, Raffaella; Gianesin, Barbara; Zappu, Antonietta; Denotti Anna, Rita; Di Giorgio Mary, Ann; Sciortino, Roberta; Motta, Irene; Panzieri Daniele, Lello; Rosso, Rosamaria; Bulla, Anna; Culcasi, Martina; Pasanisi Anna, Maria; De Franceschi, Lucia; Di Maggio, Rosario; Pinto Valeria, Maria; Sanna Paola Maria, Grazia; Ricchi, Paolo; Ruffo Giovan, Battista; Schieppati, Francesca; Roberti, Domenico; Ferrero Giovanni, Battista; De Michele, Elisa; Arcioni, Francesco; Fotzi, Ilaria; Marktel, Sarah; Poloni, Antonella; Soverini, Giulia; Testa Epifania, Rita; Cabiddu, Giusy; Fortugno, Carmelo; Gigante, Antonia; Polese, Francesca; Rapezzi, Davide; Sau, Antonella; Forni Gian, Luca; Cappellini Maria, Domenica; Longo, Filomena
Prevalence and mortality trends of hemoglobinopathies in Italy: a nationwide study
2025-01-01 Gianesin, B; Piel, Fb; Musallam, Km; Barella, S; Casale, M; Cassinerio, E; Di Maggio, R; Gigante, A; Gamberini, Mr; Graziadei, G; Lisi, R; Longo, F; Maggio, A; Origa, R; Pasanisi, A; Perrotta, S; Piga, Ag; Pinto, Vm; Rosso, R; Robello, G; Russo, G; Zecca, M; De Franceschi, L; Forni, Gl
Thalassemias and Sickle Cell Diseases in Pregnancy: SITE Good Practice.
2025-01-01 Maria Pinto, Valeria; Cima, Rosanna; Di Maggio, Rosario; Livia Alga, Maria; Gigante, Antonia; Longo, Filomena; Maria Pasanisi, Anna; Venturelli, Donatella; Cassinerio, Elena; Casale, Maddalena; Origa, Raffaella; Zanconato, Giovanni; Luca Forni, Gian; De Franceschi, Lucia
Thyroid Nodule Surveillance in Transfusion-Dependent Thalassemia: A Comparative Ultrasonographic Study
2025-01-01 Casale, M; Errico, M; Origa, R; Mureddu, P; Allosso, F; Digitale Selvaggio, L; Grande, G; Di Ludovico, C; Navarra, R; Roberti, D; Capellupo, Mc; Perrotta, S; Pasquali, D.
Transfusion strategies in thalassemia and sickle cell disease SITE-SIMTI-SIdEM Good Practice
2025-01-01 Forni Gian, Luca; Vassanelli, Aurora; De Franceschi, Lucia; Marson, Piero; Lisi, Roberto; Ostuni, Angelo; Gigante, Antonia; Origa, Raffaella; Fiorin, Francesco
Beta Thalassemia in Children: Established Approaches, Old Issues, New Non-Curative Therapies, and Perspectives on Healing
2024-01-01 Origa, Raffaella; Issa, Layal
Deferasirox film-coated tablet-associated ulcerative colitis: An emerging pattern in thalassemia patients?
2024-01-01 Piolatto, A; Gaglioti, Cm; Tesio, N; Clemente, Mg; Culcasi, M; Matrone, A; Pila, Mp; Sambataro, A; Longo, F; Origa, R; Ferrero, Gb.
Differential effects of iron chelators on iron burden and long-term morbidity and mortality outcomes in a large cohort of transfusion-dependent β-thalassemia patients who remained on the same monotherapy over 10 years
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Phenoconversion’ in adult patients with β-thalassemia
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Pretransfusion hemoglobin level and mortality in adults with transfusiondependent β-thalassemia
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl.
Revisiting iron overload status and change thresholds as predictors of mortality in transfusion-dependent β-thalassemia: a 10-year cohort study
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Unplanned pregnancy in women with beta-thalassaemia treated with luspatercept
2024-01-01 Zaccheddu, E; Zappu, A; Barella, S; Clemente, Mg; Orecchia, V; Pilia, Mp; Piras, S; Pitturru, C; Scarano, M; Origa, R.
Atrial Fibrillation Prevalence and Its Management in Transfusion-Dependent Thalassemias: The Fathal Study
2023-01-01 Di Stefano, Valeria; Gianesin, Barbara; Bertini, Matteo; Culcasi, Martina; Rita Denotti, Anna; Derchi, Giorgio; Giuditta, Marianna; Longo, Filomena; Regina Manca, Maria; Cristina Martinoli, Maria; Orecchia, Valeria; Origa, Raffaella; Motta, Irene
Hepatitis C and Thalassemia: A Story with (Almost) a Happy Ending
2023-01-01 Origa, Raffaella
| Titolo | Data di pubblicazione | Autore(i) | Rivista | Editore |
|---|---|---|---|---|
| A Combination of Plerixafor and Filgrasting Promotes Successful CD34+ Cell Collection for CRISPR/Cas9 Therapy in Sickle Cell Disease Patients With Insufficient Response to Plerixafor Alone. | 1-gen-2026 | Arcioni, F; Bonetti, M; Sau, A; Zecca, M; Alzahrani, M; Alahmari, B; Alsadi, H; Almozaini, A; Ahmed, M; Essa, M; Perotti, C; Del Fante, C; Passeri, C; Iuliani, O; Russo, Ac; Di Ianni, M; Marchesi, M; Pasqua, Bl; Onorato, M; Berchicci, L; Pierini, A; Zei, T; Iacucci, R; Cerri, C; Gurdo, G; Innocente, A; Capolsini, I; Gorello, P; Colombatti, R; Origa, R; Caniglia, M. | AMERICAN JOURNAL OF HEMATOLOGY | - |
| Atrial fibrillation prevalence and its management in aging transfusion-dependent thalassemia patients: the FATHAL study | 1-gen-2026 | Di Stefano, V; Gianesin, B; Orecchia, V; Longo, F; Susanna, B; Barone, A; Culcasi, M; Denotti, Ar; Costantini, S; Ferrara, F; Foggetti, I; Gigante, A; Manca, Mr; Mazzi, F; Pasanisi, A; Pisaniello, M; Ricchi, P; Serra, M; Origa, R; Bertini, M; Motta, I. | BLOOD ADVANCES | - |
| Pregnancy and childbirth in women with thalassemia: past and present | 1-gen-2026 | Demurtas, A; Gianesin, B; Zappu, A; Cassinerio, E; Leoni, S; Ricchi, P; Fatigati, C; Ruffo, G; Miciotto, F; Roberti, D; Tartaglione, I; Pasanisi, A; Longo, F; Sorrentino, F; Salvo, A; De Franceschi, L; Lisi, R; Murgia, M; Pisano, V; Sanna, P; Testa, E; Atzeni, I; Mariani, R; Valentini, C; Arcioni, F; Barcella, L; Culcasi, M; Vitucci, A; Miulli, E; Pugliese, P; Fotzi, I; Paci, C; Barella, S; Gigante, A; Forni, G; Origa, R | HAEMATOLOGICA | - |
| Real-world evidence supports the safety and efficacy profile of luspatercept in clinically complex and heavily iron-overloaded patients | 1-gen-2026 | Gianesin, B; Zappu, A; Ferrero, Gb; Gaglioti, Cm; Santodirocco, M; Fania, G; Graziadei, G; Panzieri, Dl; Massa, A; Mina, T; Polese, F; Vitucci, A; Arcioni, F; Putti, Mc; Cecinati, V; Fotzi, I; Sanna, Pmg; Cappello, A; Longo, F; Lisi, R; Pasanisi, A; Pietrasanta, D; Bocchia, M; Bertoni, E; Cossu, A; Serra, M; Barella, S; Gigante, A; Forni, Gl; Origa, R. | BRITISH JOURNAL OF HAEMATOLOGY | - |
| The Emerging Role of Liver Stiffness Measurement in Transfusion Dependent Thalassemia. | 1-gen-2026 | Gianesin, B; Ferrero, Gb; Longo, F; Barella, S; Origa, R; Lisi, R; Pasanisi, A; Bacigalupo, L; De Franceschi, L; Forni, Gl. | AMERICAN JOURNAL OF HEMATOLOGY | - |
| Long-term efficacy and safety of luspatercept for the treatment of anaemia in patients with transfusion-dependent β-thalassaemia (BELIEVE): final results from a phase 3 randomised trial | 1-gen-2025 | Domenica Cappellini, Maria; Viprakasit, Vip; Georgiev, Pencho; D Coates, Thomas; Origa, Raffaella; Khelif, Abderrahim; Liew, Hong-Keng; Tantiworawit, Adisak; Chew, Lee-Ping; Khalil, Abdalla; Joy Ho, P; M Kuo, Kevin H; Holot, Natalia; Perin, Martina; Carolina Giuseppi, Ana; Kuo, Wen-Ling; Lai, Yinzhi; Felber Medlin, Loyse; Moro Bueno, Luciana; Kattamis, Antonis; T Taher, Ali | THE LANCET. HAEMATOLOGY | - |
| Luspatercept for Transfusion-Dependent Beta-Thalassemia: Real-World Experience in a Large Cohort of Patients From Italy | 1-gen-2025 | Origa, Raffaella; Gianesin, Barbara; Zappu, Antonietta; Denotti Anna, Rita; Di Giorgio Mary, Ann; Sciortino, Roberta; Motta, Irene; Panzieri Daniele, Lello; Rosso, Rosamaria; Bulla, Anna; Culcasi, Martina; Pasanisi Anna, Maria; De Franceschi, Lucia; Di Maggio, Rosario; Pinto Valeria, Maria; Sanna Paola Maria, Grazia; Ricchi, Paolo; Ruffo Giovan, Battista; Schieppati, Francesca; Roberti, Domenico; Ferrero Giovanni, Battista; De Michele, Elisa; Arcioni, Francesco; Fotzi, Ilaria; Marktel, Sarah; Poloni, Antonella; Soverini, Giulia; Testa Epifania, Rita; Cabiddu, Giusy; Fortugno, Carmelo; Gigante, Antonia; Polese, Francesca; Rapezzi, Davide; Sau, Antonella; Forni Gian, Luca; Cappellini Maria, Domenica; Longo, Filomena | AMERICAN JOURNAL OF HEMATOLOGY | - |
| Prevalence and mortality trends of hemoglobinopathies in Italy: a nationwide study | 1-gen-2025 | Gianesin, B; Piel, Fb; Musallam, Km; Barella, S; Casale, M; Cassinerio, E; Di Maggio, R; Gigante, A; Gamberini, Mr; Graziadei, G; Lisi, R; Longo, F; Maggio, A; Origa, R; Pasanisi, A; Perrotta, S; Piga, Ag; Pinto, Vm; Rosso, R; Robello, G; Russo, G; Zecca, M; De Franceschi, L; Forni, Gl | HAEMATOLOGICA | - |
| Thalassemias and Sickle Cell Diseases in Pregnancy: SITE Good Practice. | 1-gen-2025 | Maria Pinto, Valeria; Cima, Rosanna; Di Maggio, Rosario; Livia Alga, Maria; Gigante, Antonia; Longo, Filomena; Maria Pasanisi, Anna; Venturelli, Donatella; Cassinerio, Elena; Casale, Maddalena; Origa, Raffaella; Zanconato, Giovanni; Luca Forni, Gian; De Franceschi, Lucia | JOURNAL OF CLINICAL MEDICINE | - |
| Thyroid Nodule Surveillance in Transfusion-Dependent Thalassemia: A Comparative Ultrasonographic Study | 1-gen-2025 | Casale, M; Errico, M; Origa, R; Mureddu, P; Allosso, F; Digitale Selvaggio, L; Grande, G; Di Ludovico, C; Navarra, R; Roberti, D; Capellupo, Mc; Perrotta, S; Pasquali, D. | JOURNAL OF CLINICAL MEDICINE | - |
| Transfusion strategies in thalassemia and sickle cell disease SITE-SIMTI-SIdEM Good Practice | 1-gen-2025 | Forni Gian, Luca; Vassanelli, Aurora; De Franceschi, Lucia; Marson, Piero; Lisi, Roberto; Ostuni, Angelo; Gigante, Antonia; Origa, Raffaella; Fiorin, Francesco | BLOOD TRANSFUSION | - |
| Beta Thalassemia in Children: Established Approaches, Old Issues, New Non-Curative Therapies, and Perspectives on Healing | 1-gen-2024 | Origa, Raffaella; Issa, Layal | JOURNAL OF CLINICAL MEDICINE | - |
| Deferasirox film-coated tablet-associated ulcerative colitis: An emerging pattern in thalassemia patients? | 1-gen-2024 | Piolatto, A; Gaglioti, Cm; Tesio, N; Clemente, Mg; Culcasi, M; Matrone, A; Pila, Mp; Sambataro, A; Longo, F; Origa, R; Ferrero, Gb. | BRITISH JOURNAL OF HAEMATOLOGY | - |
| Differential effects of iron chelators on iron burden and long-term morbidity and mortality outcomes in a large cohort of transfusion-dependent β-thalassemia patients who remained on the same monotherapy over 10 years | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | BLOOD CELLS, MOLECULES, & DISEASES | - |
| Phenoconversion’ in adult patients with β-thalassemia | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | AMERICAN JOURNAL OF HEMATOLOGY | - |
| Pretransfusion hemoglobin level and mortality in adults with transfusiondependent β-thalassemia | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl. | BLOOD | - |
| Revisiting iron overload status and change thresholds as predictors of mortality in transfusion-dependent β-thalassemia: a 10-year cohort study | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | ANNALS OF HEMATOLOGY | - |
| Unplanned pregnancy in women with beta-thalassaemia treated with luspatercept | 1-gen-2024 | Zaccheddu, E; Zappu, A; Barella, S; Clemente, Mg; Orecchia, V; Pilia, Mp; Piras, S; Pitturru, C; Scarano, M; Origa, R. | BRITISH JOURNAL OF HAEMATOLOGY | - |
| Atrial Fibrillation Prevalence and Its Management in Transfusion-Dependent Thalassemias: The Fathal Study | 1-gen-2023 | Di Stefano, Valeria; Gianesin, Barbara; Bertini, Matteo; Culcasi, Martina; Rita Denotti, Anna; Derchi, Giorgio; Giuditta, Marianna; Longo, Filomena; Regina Manca, Maria; Cristina Martinoli, Maria; Orecchia, Valeria; Origa, Raffaella; Motta, Irene | BLOOD | - |
| Hepatitis C and Thalassemia: A Story with (Almost) a Happy Ending | 1-gen-2023 | Origa, Raffaella | PATHOGENS | - |